There are 2 kinds of treatment for Gaucher disease type 1. Treatment outcomes may vary among patients.
Substrate reduction therapy (SRT): Oral capsule
- Reduces the amount of GL-1 produced
- Oral medicine taken daily
Enzyme replacement therapy (ERT): Infusion
- Adds a modified version of the enzyme that helps your body break down GL-1
- Intravenous (IV) infusion usually given every 2 weeks at an infusion center, a doctor’s office, or at home as medically appropriate. (Each infusion takes approximately 1 to 2 hours.)
Do not ignore the signs and symptoms of GD1. Regardless of disease severity, it is important to diagnose GD1 and start disease management as soon as possible.
Once you have a diagnosis of GD1, you and your doctor will determine the right treatment approach for you. The Sanofi CareConnectPSS® team is here to help eligible patients learn more about GD1, potential treatments, and ongoing management.
Sanofi does not provide medical advice, diagnosis, or treatment. The health information contained herein is provided for general educational purposes only. Your healthcare professional is the best source of information regarding your health. Please consult your healthcare professional if you have any questions about your health or treatment.